Rare Diseases @CheckOrphan
CheckOrphan is the leading #news and information platform dedicated to #rarediseases and #orphandrugs checkorphan.org Santa Cruz, USA / Basel, CH Joined April 2009-
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Monopar Announces Publication of Phase 2 Study Demonstrating ALXN1840 Significantly Improves Copper Balance in Patients with Wilson Disease - For More Information Visit shorturl.at/XfmhN @MonoparTx #Wilson_Disease #Rare_Diseases #Orphan_Drugs #Drug_research
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Savara Presents Long-Term IMPALA-2 Data Showing Sustained Efficacy and Safety of Molgramostim in aPAP at ATS 2026 Conference - For More Information Visit shorturl.at/sOouQ @SavaraPharma #Rare_Diseases #aPAP #Autoimmune_Pulmonary_Alveolar_Proteinosis #Orphan_Drugs
CSL Canada Announces First Canadian Patient Receives HEMGENIX® (etranacogene dezaparvovec) Hemophilia B Gene Therapy in Ontario, Canada - For More Information Visit shorturl.at/NsRt5 #HemophiliaB #Rare_Diseases #Orphan_Drugs #HEMGENIX #Drug_Research @CSL
Dyne Therapeutics Initiates Phase 3 FORZETTO Trial of Zeleciment Rostudirsen for Duchenne Muscular Dystrophy (DMD) - For More Information Visit shorturl.at/THW0c @Dyne_tx #Duchenne #Muscular_Dystrophy #DMD #Rare_Diseases #Orphan_Drugs #Pediatric_Diseases
Flow Pharma U.S. Patent Allowed for Broad-Spectrum Ebola Treatment Using Siltuximab and Microsphere Delivery Platform - For More Information Visit shorturl.at/7UdEh #FlowPharma #Rare_Diseases #Ebola
IntraBio Receives Regulatory Authorization to Begin Pivotal Phase III Trial of Levacetylleucine in CACNA1A-Related Disorders Across Participating Regions - For More Information Visit shorturl.at/KjBcJ @IntraBio #CACNA1A_Disorders #spinocerebellar_ataxia_6 #Rare_Diseases
Telomir Reports Peer-Reviewed Publication of Telomir-Zn Data Demonstrating Improved Survival and Multiple Endpoint Benefits in Wilson's Disease - For More Information Visit shorturl.at/8Dl83 @TelomirPharma #Wilson_Disease #Rare_Diseases #Orphan_Drugs #Telomir
A Johns Hopkins Registry Study Found CFTR Modulator Therapies Associated with a 66% Lower Hazard of Death Over Eight Years in Cystic Fibrosis - For More Information Visit shorturl.at/6XM9k #Cystic_Fibrosis #CF #Rare_Diseases #Orphan_Drugs @JohnsHopkinsSPH
Notre Dame Breakthrough Multiple Sclerosis Study Challenges Decades-Old Assumptions and Redefines the Future of Myelin Repair Research - For More Information Visit shorturl.at/0skyE @NotreDame #MS #Multiple_Sclerosis #Rare_Diseases #Orphan_Drugs #Drug_research
New England Journal of Medicine Publishes TETON-1/2 Results Showing Nebulized Tyvaso Significantly Improves Outcomes in Idiopathic Pulmonary Fibrosis - For More Information Visit shorturl.at/nAtHF #NEJM #IPF #Idiopathic_Pulmonary_Fibrosis #Rare_Diseases #Orphan_Drugs
Zenas BioPharma to Present Positive Phase 3 INDIGO Trial Results for Obexelimab in IgG4-Related Disease at EULAR 2026 Congress - For More Information Visit shorturl.at/Av858 #Zenas_BioPharma #EULAR #IgG4_RD #IgG4_Related_Disease #Rare_Diseases #Orphan_Drugs
Cullinan Therapeutics Receives FDA Orphan Drug Designation for CLN-049, a Novel FLT3xCD3 T Cell Engager, in R/R Acute Myeloid Leukemia - For More Information Visit shorturl.at/93Oun @CullinanTx #AML #FDA #Acute_Myeloid_Leukemia #Leukemia #Rare_Diseases
Korro Selects KRRO-111 as Development Candidate for the Potential Treatment of Alpha-1 Antitrypsin Deficiency (AATD) - For More Information Visit shorturl.at/lT908 @KorroBio #Alpha1_Antitrypsin_Deficiency #AATD #Rare_Diseases #Orphan_Drugs #Korro_Bio #Drug_research
Tiziana Life Sciences Announces New Positive Clinical Data for Intranasal Foralumab in Non-Active Secondary Progressive Multiple Sclerosis - For More Information Visit shorturl.at/QoeV0 #Tiziana_Life_Sciences #Multiple_Sclerosis #SPMS #Rare_Diseases #Orphan_Drugs
Egetis to Present Healthcare Resource Drivers and Cost in MCT8 Deficiency at ISPOR 2026 - For More Information Visit shorturl.at/mEeKO #ISPOR @Egetis_EGTX #MCT8_Deficiency #Rare_Diseases #Orphan_Drugs #Drug_research #Allan_Herndon_Dudley_syndrome #AHDS
Amplia Therapeutics Launches First Stage of Registration-Enabling Trial of Narmafotinib in Pancreatic Cancer - For More Information Visit shorturl.at/8PqWK @ampliatx #Pancreatic_Cancer #Rare_Diseases #FDA #Orphan_Drugs #Cancer_Research #Amplia_Therapeutics
FDA Accepts AQNEURSA® sNDA and Grants Priority Review for Ataxia-Telangiectasia in Adults and Pediatric Patients - For More Information Visit shorturl.at/8hyGI @IntraBio #Ataxia_Telangiectasia #Rare_Diseases #FDA #Orphan_Drugs #Drug_research #Pediatric_Disorders
Lantern Pharma Announces Successful Outcome of FDA Type C Meeting Request for HARMONIC™ Phase 2 Trial of LP-300 in Never-Smokers with NSCLC - For More Information Visit shorturl.at/gIeF7 @LanternPharma #FDA #NSCLC #Lung_Cancer #Rare_Diseases #Orphan_Drugs
Alterity Therapeutics Highlights Promising Phase 2 Multiple System Atrophy (MSA) Data and Advances ATH434 Toward Phase 3 Development - For More Information Visit shorturl.at/xjxUD @AlterityT #MSA #FDA #Multiple_System_Atrophy #Rare_Diseases #Orphan_Drugs
Design Therapeutics Reports Positive Phase 1/2 Data for DT-216P2 in Friedreich Ataxia Showing Biomarker and Clinical Improvements - For More Information Visit shorturl.at/XqkHU #Design_Therapeutics #Rare_Diseases #Friedreich_Ataxia #Orphan_Drugs #Drug_research
Rare Disease Day @rarediseaseday
42K Followers 3K Following 28 February 2027 is Rare Disease Day. Raising awareness for patients, families and carers around the world that are impacted by rare diseases. #RareDiseaseDay
EURORDIS-Rare Disease... @eurordis
31K Followers 1K Following An alliance of over 1,000 patient organisations working across borders and diseases to improve the lives of all people living with rare diseases.
RARE Revolution Magaz... @RareRevolutionM
12K Followers 7K Following Digital magazine giving a voice to those affected by rare conditions and the charities that support them. Contact us: [email protected]
Beacon for Rare Disea... @RareBeacon
12K Followers 10K Following Beacon is a UK-based charity that is building a united rare disease community with patient groups at its heart. Previously known as Findacure.
Effie Parks @OnceUponAGene
7K Followers 4K Following Rare Disease Advocate | Award Winning Podcaster | Speaker | Captain Connection | RareMama to my sweet, Ford, who lives with #CTNNB1 🦓
National Organization... @RareDiseases
40K Followers 3K Following #NORD has been the voice of the U.S. #RareDisease community for 40+ years strong. Official U.S. sponsor of #RareDiseaseDay. On Bluesky at @ https://t.co/D7PIT4k0Py
FEDER | Enfermedades ... @FEDER_ONG
39K Followers 8K Following 👉🏻 Somos la esperanza de 3 millones de personas con #enfermedadesraras 🍀 Representamos a 442 organizaciones de pacientes y a 1.546 patologías poco frecuentes
Cambridge Rare Diseas... @camraredisease
8K Followers 6K Following Improving outcomes for those living with rare conditions. Also find us at: https://t.co/kZWskP9Ojj
Global Genes @GlobalGenes
29K Followers 6K Following Empowering the Next Generation Rare Disease Advocate. Merged with RARE-X Dec. 2022. #CareAboutRare
Patient Worthy @PatientWorthy
8K Followers 7K Following We're a resource for engaging, informative content and rare patient news, well done.
The Journal of Inheri... @JIMD_Editors
3K Followers 819 Following At a recent Council meeting a decision was made that the SSIEM will no longer interact with X. Please find us on any other Social Media channel.
Ethan Perlstein 1-to-... @eperlste
19K Followers 2K Following ceo @1000cures, ceo @PerlaraPBC (w16 @ycombinator), founder @epalrestat, founder @endrarediseases, founder @smer28rapa
RarasNoInvisibles @NoInvisibles
55K Followers 7K Following Hablamos de salud, enfermedades raras, inclusion social y biomedicina. Escribe @Sombradoble Mas Información: [email protected]
Rare Patient Voice @rarepatientvoic
2K Followers 3K Following We help clients find rare & non-rare disease patients & caregivers for research studies, & connect patients & caregivers with paid research opportunities.
ERDERA @ERDERA_org
4K Followers 2K Following The European Rare Diseases Research Alliance. Co-funded by European Union's @HorizonEU Research & Innovation programme. Views expressed are of authors only.
Genetic Alliance UK @GeneticAll_UK
15K Followers 2K Following National charity working for everyone affected by genetic, rare and undiagnosed conditions. We run the campaign Rare Disease UK and support network @SWAN_UK.
Yoni - יוני (and ... @Primary_Immune
48K Followers 28K Following Proud Jew. Proud Israeli. Immigrated to Israel from USA. הודו לה' כי טוב כי לעולם חסדו offline every Shabbat
Alvaro Hermida @Info_Rares
2K Followers 1K Following Specialist on Metabolic Diseases and always looking on the bright side of life.
FamilieSCN2A @FamilieSCN2A
2K Followers 1K Following Our vision is to find effective treatments and a cure for SCN2A disorders.
Stephanie Fischer @RarePOV
7K Followers 5K Following #Raredisease patient advocate & #stroke survivor.🦓 Member of @PARareDisease. Opinions are my own.
AYOUB HUSSEIN @kakolla_1
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JS @javiersantosw
472 Followers 306 Following Molecular Biologist. PhD. Leading a Protein Research Lab on Rare Diseases at Buenos Aires University.
HemeHub @HemeHub
289 Followers 137 Following HemeHub | Supporting hematology by enhancing care, driving innovation, and advancing research & treatment strategies.
Fortune Nathaniel @Fortuneecolab
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Håkan Göranson @hakangoranson
0 Followers 18 Following SCA patient sharing hope & stories. Founder of Symrem - nutraceutical symptom relief for ataxia. Join us: https://t.co/pp0X8w8Lmg
HealthVector AI @HealthVectorAI
13 Followers 184 Following Biotech signals, not headlines. Translating clinical data, FDA decisions, and market moves into what actually matters.
Seyhun Saçlı @SaclSeyhun
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Alissa @Alissa3397
1 Followers 159 Following
Fahreddin Palaz, MD @CRISPRvs
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Parwez Eshaan پرو�... @theparwezeshaan
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RyuStrong_DMD @RyuStrong_DMD
11 Followers 108 Following DMD warrior and Mom advocacy team putting Jesus first while fighting for kids with DMD and access to treatments they deserve. #EndDuchnne #RareDiseaseKidsRise
[email protected] @veggyluvr
1 Followers 124 Following
Peter Törngren @peter_torngren
718 Followers 3K Following Gillar börs, index, analyser. Tweets är inte råd utan endast jag som ventilerar mina privata tankar. Fil kand i Systemvetenskap och Ek kand i Företagsekonomi.
Athena Beta @BetaathenaOrg
0 Followers 17 Following
AReally @AndreaRilli
80 Followers 1K Following
Dhrupad Panchal @panchal_dhrupad
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Sarah Rice @ricecakes0913
357 Followers 3K Following My tendency to make up stories&lie compulsively for the sake of my own amusement takes up a good portion of my day -ChelseaHandler #ΦΜ #HTTR #teamrage #lacrosse
KaylaVecera @KFC_Rx
20 Followers 135 Following
Paula Kravetz @pmarchesehay
1 Followers 51 Following
TARUN KHARI @khari_555
42 Followers 218 Following 🇮🇳 Every Problem has a Solution but that Solution is next problem.#bitcoin
IMC @IMCURU
177 Followers 4K Following
TUSC3 Rare @TUSC3CDG
12 Followers 567 Following Helping to bring awareness and the latest research on TUSC3-CDG / TUSC3 ARID.
Sylvia Smith @Zylvia2A
477 Followers 3K Following
Francesca Magrinelli @FraMagrinelli
980 Followers 522 Following MD, PhD Senior Clinical Research Fellow & Honorary Consultant Neurologist UCL Queen Square Institute of Neurology @UCLIoN Movement Disorders Neurogenetics
Antonio López @AntonioLopez82
168 Followers 460 Following
AbbVie Oncology Medic... @AbbVieUSOncMed
291 Followers 260 Following Dedicated to communicating emerging science from AbbVie in Oncology. Please see our community guidelines: https://t.co/QNcTOBdm6Y. Intended for US HCPs only.
Dr. Kash Sarabi @drkashsarabi
2K Followers 3K Following I stand with Elon Musk and Dr. Patrick Soon‑Shiong. Giving others a chance to fight cancer. Let’s team up for a podcast/Spaces here on X —DM me if interested!
Dr Adam @DrAdamTate
2K Followers 4K Following Senior Lecturer in Curriculum & Assessment @Arden_Uni | #Founder @FahrBeyond | #Director @IPATH2010 | Alumnus @UniofOxford @brookes_edu #HigherEd | views mine
Rare disease faundati... @RareDieaseIR
14 Followers 91 Following The Rare Diseases Foundation of Iran is an organization dedicated to supporting patients with rare diseases, advocating for their rights, and raising awareness.
Bio Pharma @biopharma96
3 Followers 85 Following
rareobesitynews @rareobesitynews
0 Followers 35 Following
Shane morris @Shanemorrifb7t
2 Followers 199 Following I was Diagnosed with Ataxia last August. I am still having testing for FA....I am still understanding it and love hearing other people's stores on it as well
Alterity Therapeutics @AlterityT
280 Followers 19 Following Creating an alternate future for people living with #NeurodegenerativeDiseases
Jessica March @JessicaBMarch
0 Followers 25 Following
Karen @Kay200495
18 Followers 128 Following
Jana @jboremski
31 Followers 147 Following
Zweitmeinung @zweitmeinung2
234 Followers 2K Following
David @KiefChief69
169 Followers 924 Following I’m just happy to be here. Alpha scavenger and occasional cringe lord. Trying to be less retarded, progress is volatile. Financial advice.
Adu Subramanian @plainyogurt21
8K Followers 602 Following Future MD, Bioengineer, Investor, Member at https://t.co/NNDdxGpyIH, Call Leader @Slingshot_Invst, https://t.co/ajZINo1LRZ, https://t.co/r0FcNbuy2U
Kenny @Kennydoesbio
3K Followers 1K Following On the hunt for bio plays & big fish, looking for buyside roles (DMs open)
AB @111biotech
40 Followers 713 Following
Rare Disease Day @rarediseaseday
42K Followers 3K Following 28 February 2027 is Rare Disease Day. Raising awareness for patients, families and carers around the world that are impacted by rare diseases. #RareDiseaseDay
EURORDIS-Rare Disease... @eurordis
31K Followers 1K Following An alliance of over 1,000 patient organisations working across borders and diseases to improve the lives of all people living with rare diseases.
RARE Revolution Magaz... @RareRevolutionM
12K Followers 7K Following Digital magazine giving a voice to those affected by rare conditions and the charities that support them. Contact us: [email protected]
Beacon for Rare Disea... @RareBeacon
12K Followers 10K Following Beacon is a UK-based charity that is building a united rare disease community with patient groups at its heart. Previously known as Findacure.
Effie Parks @OnceUponAGene
7K Followers 4K Following Rare Disease Advocate | Award Winning Podcaster | Speaker | Captain Connection | RareMama to my sweet, Ford, who lives with #CTNNB1 🦓
Raras pero Reales @RarasReales
13K Followers 3K Following Sanofi, comprometidos con el descubrimiento de terapias para pacientes con #EnfermedadesRaras. https://t.co/wduV3mGwsQ
National Organization... @RareDiseases
40K Followers 3K Following #NORD has been the voice of the U.S. #RareDisease community for 40+ years strong. Official U.S. sponsor of #RareDiseaseDay. On Bluesky at @ https://t.co/D7PIT4k0Py
FEDER | Enfermedades ... @FEDER_ONG
39K Followers 8K Following 👉🏻 Somos la esperanza de 3 millones de personas con #enfermedadesraras 🍀 Representamos a 442 organizaciones de pacientes y a 1.546 patologías poco frecuentes
Cambridge Rare Diseas... @camraredisease
8K Followers 6K Following Improving outcomes for those living with rare conditions. Also find us at: https://t.co/kZWskP9Ojj
Global Genes @GlobalGenes
29K Followers 6K Following Empowering the Next Generation Rare Disease Advocate. Merged with RARE-X Dec. 2022. #CareAboutRare
Patient Worthy @PatientWorthy
8K Followers 7K Following We're a resource for engaging, informative content and rare patient news, well done.
Ethan Perlstein 1-to-... @eperlste
19K Followers 2K Following ceo @1000cures, ceo @PerlaraPBC (w16 @ycombinator), founder @epalrestat, founder @endrarediseases, founder @smer28rapa
RarasNoInvisibles @NoInvisibles
55K Followers 7K Following Hablamos de salud, enfermedades raras, inclusion social y biomedicina. Escribe @Sombradoble Mas Información: [email protected]
Rare Patient Voice @rarepatientvoic
2K Followers 3K Following We help clients find rare & non-rare disease patients & caregivers for research studies, & connect patients & caregivers with paid research opportunities.
ERDERA @ERDERA_org
4K Followers 2K Following The European Rare Diseases Research Alliance. Co-funded by European Union's @HorizonEU Research & Innovation programme. Views expressed are of authors only.
Genetic Alliance UK @GeneticAll_UK
15K Followers 2K Following National charity working for everyone affected by genetic, rare and undiagnosed conditions. We run the campaign Rare Disease UK and support network @SWAN_UK.
Yoni - יוני (and ... @Primary_Immune
48K Followers 28K Following Proud Jew. Proud Israeli. Immigrated to Israel from USA. הודו לה' כי טוב כי לעולם חסדו offline every Shabbat
Stephanie Fischer @RarePOV
7K Followers 5K Following #Raredisease patient advocate & #stroke survivor.🦓 Member of @PARareDisease. Opinions are my own.
Rare Disease UK @rarediseaseuk
20K Followers 2K Following National campaign run by @GeneticAll_UK to improve the lives of those affected by rare conditions and all who support them. #RareDisease.
Luke Rosen @lukebrosen
2K Followers 423 Following Founder of https://t.co/GkrwXhfkoy and https://t.co/eWtcezWeJc. Firefighter. Works with families affected by neurological diseases and cancer. Baseball and hockey. Proud dad.
Korro Bio @KorroBio
522 Followers 130 Following We are a leading RNA editing company focused on the discovery and delivery of novel genetic medicines.
Egetis Therapeutics @Egetis_EGTX
392 Followers 85 Following Egetis is an innovative pharmaceutical drug development company, focusing on projects in late-stage development for treatment of serious rare diseases.
Amplia Therapeutics @ampliatx
447 Followers 55 Following Amplia Therapeutics Limited (ASX:ATX) is a Melbourne-based biopharmaceutical company focused on the clinical development of novel oncology drugs.
Tenaya Therapeutics @TenayaThera
669 Followers 118 Following Scaling new heights in the fight against heart disease.
Tevard Biosciences @TevardB
231 Followers 501 Following
BlossomHill Therapeut... @bhtherapeutics
49 Followers 30 Following BlossomHill Therapeutics, Inc. is a small molecule drug discovery and development company focused on unmet medical needs in oncology and autoimmune disorders.
Zai Lab @ZaiLab_Global
587 Followers 218 Following Zai Lab is an innovative biopharmaceutical company based in China and the U.S., focused on delivering transformational outcomes to patients around the world.
AskBio Inc. (AskBio) @ask_bio
1K Followers 273 Following AskBio is a leading clinical-stage gene therapy company dedicated to improving the lives of patients with rare diseases and other disorders.
Inhibrx Biosciences, ... @inhibrx
112 Followers 5 Following Innovation Focused Outcomes Driven Biotechnology Research
Anixa Biosciences @AnixaBio
586 Followers 145 Following Anixa Biosciences (NASDAQ: $ANIX) is focused on the treatment and prevention of cancer.
Servier Pharmaceutica... @ServierPharma
827 Followers 917 Following Servier Pharmaceuticals is a U.S. subsidiary of Servier with a focus on oncology treatment and care. See our community guidelines here: https://t.co/tHNeTw4iGH
Actio Biosciences @actiobiosci
44 Followers 2 Following Bringing meaningful therapies from one to many.
Hospital Sant Joan de... @SJDbarcelona_es
28K Followers 1K Following Hospital materno infantil de alta especialización. Contacta en https://t.co/ad5SDMJg6y
Repertoire Immune Med... @RepertoireIM
260 Followers 197 Following Repertoire is a biotechnology company creating a new category of immune medicines for cancer and autoimmune disease.
Pancreas Verona @PancreasVerona
4K Followers 247 Following The official Twitter account of the Unit of Pancreatic Surgery at the University of Verona Hospital Trust, Italy
City Therapeutics @CityTx_
138 Followers 0 Following Leading the next-generation of RNAi trigger molecule engineering to develop a pipeline of disruptive medicines.
CIBIO - UniTrento @CIBIO_UniTrento
2K Followers 474 Following The Department of Cellular, Computational and Integrative Biology at the University of Trento, Italy. 📽 YouTube channel: https://t.co/RPwEJ3f7Zb
Ernexa Therapeutics @ErnexaTx
21 Followers 5 Following Ernexa Therapeutics (NASDAQ: ERNA) is developing innovative cell therapies for the treatment of advanced cancer and autoimmune diseases.
Northwell Health @NorthwellHealth
24K Followers 534 Following We are more than a health system — We are 104,000+ people looking at #healthcare differently and working to #RaiseHealth for all. 💪
Nano Viricides @NNVCNYSE
197 Followers 500 Following NanoViricides, Inc. is a global leader in the development of nanomedicine drugs against viruses. NYSE:NNVC
Alpha Tau Medical @AlphaTauMedical
1K Followers 3K Following Alpha DaRT enables high-precision alpha radiation for solid #cancer. Radium-224-based alpha #radiotherapy kills the #tumor while sparing healthy tissue #radonc
SetPoint Medical @SetPointMed
594 Followers 43 Following A revolutionary new treatment for rheumatoid arthritis. #StartActivating #SetPointSystem #SetPointTherapy Individual outcomes vary. Safety info: https://t.co/BhikdgoQHO
Prothena Corporation @ProthenaCorp
792 Followers 45 Following Prothena is a late-stage clinical biotech company with expertise in protein dysregulation; pipeline in neurodegenerative and rare peripheral amyloid diseases
SecuraBio @SecuraBio
57 Followers 6 Following
Compass Therapeutics @compassbio
189 Followers 10 Following Developing next-generation antibodies into transformative cancer therapies that improve patients’ lives.
Yale School of Medici... @YaleMed
160K Followers 886 Following The official X feed for Yale School of Medicine, a world-renowned center for biomedical research, education, and health care founded in 1810.
Seed Therapeutics @seedtx
52 Followers 0 Following Seed Therapeutics is a global research company focused on harnessing and engineering molecules that use “molecular glues” to attack protein targets.
Charité - Universit�... @ChariteBerlin
62K Followers 243 Following Dies ist der offizielle X-Account der Charité. Hier postet, moderiert und kommentiert das Social-Media-Team.
Star Therapeutics @STAR_Biotech
38 Followers 8 Following Developing life-changing therapies for as many rare diseases as possible for the millions of patients in urgent need.
TME Pharma @tme_pharma
813 Followers 242 Following A clinical-stage biotechnology company specializing in the development of novel therapies for cancer and eye diseases. Listed on Euronext Growth Paris.
Rivus Pharmaceuticals @RivusPharma
285 Followers 61 Following Rivus is a clinical-stage biopharmaceutical company advancing novel medicines for obesity and the resulting chronic cardiometabolic diseases.
GalmedPharmaceutical @GalmedPharma
4K Followers 2K Following Galmed is a clinical-stage biopharmaceutical company focused on the development of a novel, once-daily, oral therapy for the treatment of liver diseases.
Global Coalition for ... @GCAResearch
1K Followers 1K Following GCAR is a 501(c)(3) non-profit corporation pioneering collaborative, innovative clinical trials to speed the discovery and development of cures
Anumana | AI in Cardi... @anumanainc
434 Followers 44 Following Harnessing the power of the electrical signal of the heart to transform cardiac care through cutting-edge AI solutions
Autonomix Medical @AutonomixMed
276 Followers 133 Following Autonomix is focused on advancing innovative technologies to revolutionize how diseases involving the nervous system are diagnosed and treated. Nasdaq: $AMIX
Neuropacs, Corp. @neuropacs
5 Followers 3 Following
Context Therapeutics @Context_Tx
481 Followers 576 Following Advancing T Cell Engagers for Solid Tumors
Caris Life Sciences @carisls
23K Followers 3K Following Caris Life Sciences, the precision medicine pioneer, develops and delivers innovative solutions to revolutionize healthcare and improve the human condition.
Glycomine Bio @GlycomineBio
51 Followers 23 Following We are developing GLM101, a novel substrate replacement therapy for #PMM2CDG, a congenital disorder of #glycosylation and #raredisease.
CellCentric @CellCentric
695 Followers 375 Following Inobrodib (CCS1477): first-in-class p300/CBP small molecule inhibitor drug, to treat specific cancers.
Université de Montpe... @umontpellier
18K Followers 2K Following 🧑🎓 52.372 étudiants 🏫 17 facs, instituts, écoles ⚗ 73 structures de recherche 🎓 657 diplômes 🔝 200 meilleures universités mondiales
TRIANA Bio @Triana_Bio
208 Followers 89 Following Unlocking the full potential of molecular glues to discover and develop precision medicines to tranform patient lives.
Aligos Therapeutics @AligosThera
495 Followers 150 Following Aligos is a biopharmaceutical company developing targeted therapeutics to address unmet medical needs in liver & viral diseases like MASH, CHB and COVID-19.
Karyopharm @Karyopharm
2K Followers 703 Following Discovers, develops and commercializes life-changing cancer therapies. Fueled by a belief in the extraordinary strength and courage of patients.
Sumitomo Pharma Ameri... @SumitomoPharma
179 Followers 80 Following Sumitomo Pharma America is a science-based, technology-driven biopharmaceutical company focused on delivering therapeutic and scientific breakthroughs.
The Lancet Haematolog... @TheLancetHaem
22K Followers 2K Following The Lancet Haematology is a world-leading #haematology journal publishing peer-reviewed research and reviews, opinion, and news. #hematology
Pharvaris @pharvaris
63 Followers 1 Following Pharvaris is a late-stage company advancing novel bradykinin B2 receptor antagonists to treat and prevent hereditary angioedema (HAE) attacks. $PHVS
IntraBio @IntraBio
89 Followers 11 Following IntraBio is a late-stage biopharmaceutical company developing novel therapies for rare (“orphan”) and common neurodegenerative diseases
Remix Therapeutics @RemixThera
607 Followers 40 Following Clinical-stage #biotech company developing novel small molecule therapies designed to reprogram RNA processing and address disease drivers at their origin.
Shionogi Inc. (U.S.) @ShionogiUS
413 Followers 83 Following Shionogi Inc. is a U.S. subsidiary of Shionogi & Co., Ltd., a Japanese research-driven pharmaceutical company. Community guidelines here: https://t.co/Q2yTBvclyfYou might like
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